TRANSFORM

  • TRANSFORM MEP Charter with Solutions to Enable Safe and Timely Patient Access to Advanced Therapies in Europe

    On 13 October, the European Alliance for Transformative Therapies launched its MEP Charter with Solutions to Enable Safe and Timely Patient Access to Advanced Therapies in Europe, developed collaboratively with expert stakeholders. The Charter will serve as a guide for TRANSFORM’s action in the coming years, including for the MEPs to prepare the discussion of expected legislative files such as SoHO legislation, the General Pharmaceuticals legislations, the EHDS, among others.

    More →

  • TRANSFORM: Multi-stakeholder approach to gene and cell therapies

    TRANSFORM is a multi-stakeholder alliance composed of patient groups, medical experts and associations, healthcare and non-healthcare specialists, scientists, researchers, industry actors and other relevant stakeholders. We advocate for improving the regulatory and legislative systems with the intention to realise the promise of transformative therapies for severe, disabling or life-limiting conditions.

    About Us Contact Us

  • Policy Asks on the Regulatory Framework for ATMPs

    The European Alliance for Transformative Therapies’ (TRANSFORM) Policy Asks advocate for a regulatory framework that enables safe and timely patient access to transformative therapies, building on the 2021 TRANSFORM Recommendations for Action. 

    Read Policy Asks

  • Policy Asks on Access to Authorised ATMPs

    The European Alliance for Transformative Therapies’ (TRANSFORM) Policy Asks advocate for changes that offer potential solutions to unlock safe and timely patient access to authorised ATMPs in Europe, building on the 2021 TRANSFORM Recommendations for Action.

    Read Policy Asks

  • 5 Policy Asks to Optimize Cross-border Patient Access to Transformative Therapies

    The TRANSFORM MEP Interest Group launched 5 Policy Asks on how to optimize cross-border patient access to transformative therapies at their online event on 10 November 2021.

    Read Policy Asks Watch Event

Members

European Society of Gene and Cell Therapy (ESGCT)
ReNEW Consortium – Stem Cell Medicine
EFNA – European Federation of Neurological Associations
RI – Retina International
WDO – World Duchenne Organization
IPOPI – International Patient Organisation for Primary Immunodeficiencies
TIF – Thalassaemia International Federation
EHC – European Haemophilia Consortium
EURORDIS – Rare Diseases Europe
EPTRI – European Paediatric Translational Research Infrastructure
CCI Europe – Childhood Cancer International Europe
SIOP Europe – the European Society for Paediatric Oncology
EAHAD – European Association for Haemophilia and Allied Disorders
EU EYE – European Alliance for Vision Research and Ophthalmology
EUCOPE – European Confederation of Pharmaceutical Entrepreneurs

@TRANSFORM_CGT on Twitter Follow us →

RT @CancerPatientsE: 📣 We are calling for better use of real-world evidence to improve health outcomes! Join us and sign the Call to Action…
23 March at 4:09pm
Reply Retweet
RT @RWE4Decisions: Dr A Natz @EUCOPE shares the value of the multi-stakeholder collaboration in #RWE4Decisions and @TRANSFORM_CGT, key init…
23 March at 4:08pm
Reply Retweet
Today @ 🇪🇺 #HealthTechSummit, Dr.Natz @Eucope mentioned @TRANSFORM_CGT as a multi stakeholder platform fostering dialogue & providing recommendations on how to make the best possible use of #RWD to enable patient access to therapies ➡️see Charter Rec#3: https://t.co/XAeoSimAzh.
23 March at 4:08pm
Reply Retweet