Multi-stakeholder Alliance
The multi-stakeholder Alliance is governed by principles and values that underpin the joint working interactions, as well as the objectives and modus operandi for TRANSFORM.
Members
European Society of Gene and Cell Therapy (ESGCT)
ReNEW Consortium – Stem Cell Medicine
EFNA – European Federation of Neurological Associations
RI – Retina International
WDO – World Duchenne Organization
IPOPI – International Patient Organisation for Primary Immunodeficiencies
TIF – Thalassaemia International Federation
EHC – European Haemophilia Consortium
EURORDIS – Rare Diseases Europe
EPTRI – European Paediatric Translational Research Infrastructure
CCI Europe – Childhood Cancer International Europe
SIOP Europe – the European Society for Paediatric Oncology
EAHAD – European Association for Haemophilia and Allied Disorders
EU EYE – European Alliance for Vision Research and Ophthalmology
EUCOPE – European Confederation of Pharmaceutical Entrepreneurs
Observers
European Medicines Agency
In individual capacity:
- Marc Dooms, Senior Orphan Drug Pharmacist, University Hospitals Leuven
- Stuart Faulkner, Programme and Operations Manager at the Center for the Advancement of Sustainable Medical Innovation (CASMI), Oxford University